Our team
Built by pioneers
of genetic medicine.
Our team brings the experience and conviction to shape the next era of genetic medicine. From early gene therapy breakthroughs to the development of first-in-class mRNA vaccines and targeted therapies, we have repeatedly translated cutting-edge science from the lab to the clinic. Collectively, we have translated many advanced therapies from bench to bedside, and contributed to multiple approved genetic medicines.
Building on this foundation, we applied the same rigor to the development of our transformative delivery platform. RNA therapeutics are still at an early inflection point, and we are committed to defining a new class of medicines that expands what’s possible for patients.
Leadership Team

Ali Nahvi, PhD
Chief Technology Officer

Mike Klichinsky, PhD
Chief Scientific Officer

Ben Adler, PhD
Chief Business Officer

Raffaella Toso, PhD
VP of BD and Corporate Strategy
Board of Directors

Issi Rozen
Chairperson
General Partner,
Google Ventures

Vineeta Agarwala, MD, PhD
Director
General Partner,
a16z

Lawrence Klein, PhD
Independent Director
Oruka Therapeutics

Jeff Marrazzo
Independent Director
Spark Therapeutics

Federico Mingozzi, PhD
Director
Nava Therapeutics

James Dahlman, PhD
Director
Co-Founder and CSO,
Readout Capital

Jessica Alston, PhD
Observer
Partner,
F-Prime

Robin Praeger
Observer
Advisor,
Versant
We believe the future of genetic
medicine lies in in vivo approaches.
Scalable delivery, repeat dosing, and precise cell targeting will make these therapies broadly viable and accessible to patients. Our team brings the experience and conviction to shape the next era of genetic medicine.
Investors






Federico Mingozzi
Chief Executive Officer
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Mike Klichinsky
Chief Scientific Officer
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Ali Nahvi
Chief Technology Officer
Lorem ipsum dolor sit amet, consectetur adipiscing elit. Duis scelerisque eu leo ut pellentesque. Duis et metus vel ex consequat fermentum ut eget diam. Aenean ex sapien, ultricies at tortor eu, faucibus rhoncus risus. Cras risus dolor, feugiat ut laoreet eu, vestibulum sit amet nisi. Quisque pellentesque eros id diam consequat pretium. Pellentesque quis lorem sodales tellus auctor euismod. Suspendisse eu sollicitudin orci. Vestibulum nec ultrices nunc. Fusce sed faucibus lacus, ut molestie enim. Maecenas nec velit id purus auctor aliquet. Ut ornare quam eros, ut pulvinar leo pretium vitae. Cras pulvinar quis leo vel dapibus. Curabitur quis finibus odio. Proin bibendum ipsum id nibh mollis imperdiet. Nunc dui nisl, vestibulum a elementum eget, vehicula eu elit.
Raffaella Toso
Head of BD and Corporate Strategy
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Ben Adler
Chief Business Officer
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